making muscle wasting history

Exon Skipping Review April 2009

• Last Edited: 8 May 2009
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This review is an excellent way to start undersatnding exon skipping and also to catch up with the very latest developments. You can also view all of Günter Scheuerbrandt’s other excellent r...

Tags: exon skipping, genes, proteins, gene transfer.

dmd explanation and information

• Last Edited: 15 Jun 2009
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after spending 4 years trying to find info on how dmd works and what the treatments are, this is the best site for a simple and full explanation.the first link takes to the ygyh.org front page to ...

Tags: duchenne, dmd, genes, genetics.

Restores dystrophin-glycoprotein complex and improves sarcolemma integrity in the mdx

• Last Edited: 22 Sep 2010
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Background— More than 90% of Duchenne muscular dystrophy (DMD) patients develop cardiomyopathy, and many die of cardiac failure. Despite tremendous progress in skeletal muscle gene therapy, f...

Tags: muscular dystrophy, genes, viruses, gene therapy, microdystrophin.