karsenkane North West
GrantGolding Scotland
sarahb2205 South West
adelleeddie North East
carlybull1 South East
NeeruNM London
BackgroundMutations that disrupt the open reading frame and prevent full translation of DMD, the gene that encodes dystrophin, underlie the fatal X-linked disease Duchenne muscular dystrophy. Olig...
Tags: exon skipping, PMO, morpholino therapy.