making muscle wasting history

Summit pass pre-clinical development to Biomarin

• Last Edited: 29 May 2009
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New investor email out today, see below:Restructuring of Duchenne muscular dystrophy agreement with BioMarinSummit and BioMarin have recently restructured their agreement for the Duchenne muscular...

Tags: summit, biomarin, utrophin, utrophin upregulation, SMT C1100.

Investigating Utrophin as a therapy for Duchenne Muscular Dystrophy

• Last Edited: 30 Aug 2009
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Professor Dame Kay Davies CBE FRS FMedSciDirector MRC Functional Genomics UnitHead of Department, Physiology, Anatomy and Genetics,University of OxfordDuchenne muscular dystrophy (DMD) is caused b...

Tags: Utrophin Upregulation, Utrophin, Treatment for Duchenne, Professor Dame Kay Davies.

Crossing the Valley of Despair- A review by Dr Karl Bettelheim

• Last Edited: 30 Jul 2010
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Article submitted by Dr Karl Bettelheim published on the 3rd of June 2009Although there have been some very good studies published recently especially on the use of viruses to transfer human genes...

Tags: gene therapy, exonskipping, utrophin upregulation, immunodeficiency XSCID, EGFR gene, gefitinib.

BioMarin Announces Results for Phase 1 Clinical Study of BMN 195

• Last Edited: 2 Aug 2010
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Novato, Calif, August 2, 2010 – BioMarin Pharmaceutical Inc. (Nasdaq: BMRN) announced today that it has completed the Phase 1 clinical study of BMN 195, a small molecule utrophin up-regulator...

Tags: utrophin upregulation, Biomarin, BMN 195.