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RASRx receives orphan drug designation from FDA

Posted on: June 19th, 2017 | 0 comments

RASRx announced today that the United States Food and Drug Administration (FDA) has granted an Orphan Drug Designation (ODD) for its compound RASRx1902 for the treatment of Duchenne Muscular Dystrophy.  RASRx1902 is an oral therapy that has shown positive effects on muscle function in animal models of Duchenne.  In these models, the RASRx1902 has improved muscle strength and regeneration while decreasing muscle inflammation, degeneration, and necrosis.

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