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TheDMDRegistry is looking to raise £30,000 to maintain the Registry.
Location: London
TheDMDRegistry has raised £450.00 for Action Duchenne
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About TheDMDRegistry
THE DMD REGISTRY
We need £30,000 to improve the DMD Registry and that is why we are making an appeal to all registered families to ask for a one-off donation of £50. The DMD Registry is a service funded by Action Duchenne and will continue to be free to all users. Your generosity will go towards improvement and redevelopment of the DMD Registry.
The DMD Registry has been instrumental in recruiting patients for UK trials, such as the AVI-4658/MDEX Exon Skipping, PCT 124/Atalauren and the Prosensa/GlaxoSmithKline 24029 and there are international companies making enquiries for possible future trials. As you are aware, some trials need to recruit patients with specific genetic mutations and this can hinder international companies finding sufficient numbers in any one country, with this in mind the DMD Registry is part a global registry of patients run by TREAT-NMD allowing companies to recruit from different countries.
Previous Events [1]
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Fundraising for the DMD Registry - 01 September 2011
To raise £30,000 to improve the DMD Registry.
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actionduchenne
11:15, 08 Jun 11
The DMD Registry is a vital resource that has already helped clinical teams and biopharma to find patients for trials. Thank you also to Angela for all her hard work and great advice she offers whenever I call her.
