Edgewise Therapeutics has announced the start of an observational trial in participants with Becker Muscular Dystrophy (‘BMD’)) as assessed by …
Edgewise-funded natural history trial of Becker Muscular Dystrophy (BMD) now enrollingRead More
TREAT-NMD Statement on Stem Cell Tourism
We receive many questions from families who are interested in stem cell therapy as a potential treatment for Duchenne. Today, Treat-NMD (an …
Project that aimed to combine stem cell and CRISPR technology is a success
We’re delighted to report the successful completion of our research project in Dr Yung-Yao Lin’s laboratory at Queen Mary University of London. The …
Project that aimed to combine stem cell and CRISPR technology is a successRead More
Taking Raxone? We need your input!
The National Institute for Health and Care Excellence (NICE) is consulting on a potential new drug called Idebenone (or Raxone) which may slow …
Duchenne Science events back on the road in 2020
We've welcomed over 100 people to our Science on Tour events throughout 2019, these empowering and invaluable sessions have been a huge success and we …
