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exon skipping

You are here: Home / exon skipping

Dyne Therapeutics announce application to start exon 51 skipping clinical trial

7 December 2021 by Lynnette

Dyne Therapeutics, Inc. announced on 2nd December 2021 the submission of an Investigational New Drug (IND) application to the U.S. Food and Drug …

Dyne Therapeutics announce application to start exon 51 skipping clinical trialRead More

Golodirsen gains conditional approval in US

16 December 2019 by Neil

Sarepta Therapeutics has announced that the FDA (the medicines regular in the US) has granted accelerated approval to golodirsen.  Golodirsen, or …

Golodirsen gains conditional approval in USRead More

Duchenne Science events back on the road in 2020

5 December 2019 by Lynnette

We've welcomed over 100 people to our Science on Tour events throughout 2019, these empowering and invaluable sessions have been a huge success and we …

Duchenne Science events back on the road in 2020Read More

Wave gives suvodirsen update

19 September 2019 by Neil

Wave Life Sciences announced earlier this week that Suvodirsen has been granted fast track approval by the Federal Drug Administration (the drug …

Wave gives suvodirsen updateRead More

Sarepta issues clinical trials update

9 August 2019 by Neil

In recent press releases, Sarepta Therapeutics has given updates on their ongoing clinical trial programmes. These include exon skipping and gene …

Sarepta issues clinical trials updateRead More

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