Muscular Dystrophy News Today have reported that Sarepta Therapeutics and Invitae, a company specialising in genetic diagnostics, are …
Sarepta collaborate with Invitae to speed up diagnosis of DuchenneRead More
Thomas Blumire’s music to be performed at West Midlands concert
Music of Life Foundation is a small charity that uses music-making to advance education and improve the health and wellbeing of disabled …
Thomas Blumire’s music to be performed at West Midlands concertRead More
FDA Grants Orphan Drug Designation to Sarconeos
BIOPHYTIS have announced that the US Food and Drug administration (FDA) has granted orphan drug designation to its drug candidate, Sarconeos. In …
Solid announces upcoming pre-clinical data presentations
Solid have announced that new pre-clinical data from its Duchenne programs, including its lead gene transfer candidate, SGT-001, will be …
Solid announces upcoming pre-clinical data presentationsRead More
Teachers brave the Zipwire!
This weekend saw an amazing group of teachers and supporters from Bruntcliffe Academy take on the world's fastest, and Europe's longest …
NICE update on Eteplirsen
Following last week’s announcement that Sarepta’s exon skipping drug, Eteplirsen, had received a negative trend vote from the …
Action Duchenne announces changes and new key appointments
At Action Duchenne we aim to do our utmost to communicate the many promising Duchenne and Becker Muscular Dystrophy research projects and …
Action Duchenne announces changes and new key appointmentsRead More
Catabasis financial reports and business progress
-- MoveDMD® Trial Data Through One Year of Treatment Reinforce Edasalonexent Potential as Disease-Modifying Therapy for Duchenne Muscular …
Solid Biosciences financial results and business update
Company Finalizing Response to FDA Regarding Clinical Hold on SGT-001 Phase I/II Clinical Trial. Solid Biosciences Inc. (NASDAQ:SLDB) today reported …
Solid Biosciences financial results and business updateRead More
Changing Places, Changing Lives
This Friday, 11th May, one of our Trustees, Shelley, will be taking part in a campaign to raise awareness of the need for more Changing Places …
Wave Life Sciences financial results and update
Wave Life Sciences have announced financial results for the first quarter ended March 31, 2018, and provided a business update. “The …
Action Duchenne co-funding new research bringing new hope for Duchenne muscular dystrophy
Barts Charity and Action Duchenne have combined forces to support research into new stem cell therapies for Duchenne Muscular Dystrophy. With a …
Action Duchenne co-funding new research bringing new hope for Duchenne muscular dystrophyRead More
