Edgewise Therapeutics announced today positive 12-month topline results from the ongoing ARCH study, an open label, single-center study assessing the …
Watch the session recordings from our Annual Conference 2022. In this section, you can browse the recordings from the session “What is new in Duchenne Research?”
Latest Clinical trial updates (Gene Therapy)
Latest Clinical trial updates (outside of gene therapy) Volker Straub Mariacristina Scoto …
Update to the Standards of Care
Update to the Standards of Care -> Introduction to the Standards of Care Project and Respiratory Guidance : Michela Guglieri -> Cardiac Care of …
Question and Answer session with Pharmaceutical companies
Question and Answer session with Pharmaceutical companies. Action Duchenne invited pharmaceutical companies to participate in this Question and Answer …
Question and Answer session with Pharmaceutical companiesRead More
Latest Clinical trial updates (outside of gene therapy)
Latest Clinical trial updates (Gene Therapy) Speakers: Volker Straub and Michela Guglieri …
Latest Clinical trial updates (outside of gene therapy)Read More
What’s in the pipeline? (beyond gene therapy)
What's in the pipeline? (beyond gene therapy) -> Exon skipping :Tom Roberts -> New version of exon skipping : Linda Popplewell …
Gene Therapy 101
Gene Therapy 101 The types of gene therapy: gene addition (micro-dystrophin), exon skipping and genome editing.Speakers: Annemieke Aartsma-Rus and …
Corticosteroids in young boys with Duchenne the results of the FOR DMD study
Corticosteroids in young boys with DMD: the reCorticosteroids in young boys with DMDThe results of the FOR DMD study, a multi-centre study comparing …
Corticosteroids in young boys with Duchenne the results of the FOR DMD studyRead More
