We’re happy to announce that the MHRA (the medicines regulator in the UK) has given Promising Innovative Medicine (or PIM) status to Vamorolone as a …
Vamorolone gains Promising Innovative Medicine statusRead More
Cross Party Group meeting on Rare, Genetic and Undiagnosed Conditions
Last week Action Duchenne attended a meeting of the Cross Party Group on Rare, Genetic and Undiagnosed Conditions at the Scottish Parliament. The …
Cross Party Group meeting on Rare, Genetic and Undiagnosed ConditionsRead More
Information about Translarna MAA
We’re working with Muscular Dystrophy UK to make sure that emerging treatments for Duchenne get to those who need them, as quickly as possible. Since …
Highlighting the importance of treatments for all
We recently wrote to the Medicines and Healthcare Products Regulatory Agency (MHRA) - the UK drug regulator - to highlight the importance of …
