A drug called Translarna can help treat an underlying condition of Duchenne muscular dystrophyAction Duchenne, Duchenne Family Support Group, Muscular …
Translarna accepted by Scottish Medicines ConsortiumRead More
Translarna MAA COVID-19 update
Translarna can treat Duchenne caused by a nonsense mutation (about 10-13% of cases). The drug is available in England and Wales via a Managed Access …
Information about Translarna MAA
We’re working with Muscular Dystrophy UK to make sure that emerging treatments for Duchenne get to those who need them, as quickly as possible. Since …
CHMP Adopts Positive Opinion for the Expansion of the Translarna (ataluren) Label to Include Patients as Young as 2 Years of Age
- European Commission ratification anticipated in coming months - - Approval of the Translarna annual re-assessment also recommended by CHMP - PTC …
The impact of Translarna on our son and our family
Article by Kathy Wedell, mother of Isaac who was 13 in April 2017 when the article was written. Kathy played a leading role in the campaign …
