Thirteen members of staff from FHA completed the challenge in around eighteen hours, six hours ahead of the twenty-four hour deadline. They raised a …
FHA Wales staff present Three Peaks cheque to Action DuchenneRead More
Action Duchenne Funding Gene Therapy to Advance Treatments for Duchenne
We are thrilled to announce our funding of “UNITE-DMD”, the first gene therapy trials for Duchenne muscular dystrophy here in …
Action Duchenne Funding Gene Therapy to Advance Treatments for DuchenneRead More
An updated detailed review of our last Scotland roundtable
On Tuesday 7 February 2017, Action Duchenne hosted a Scottish roundtable at the David Lloyd centre in Edinburgh. It provided an excellent opportunity …
An updated detailed review of our last Scotland roundtableRead More
ScOT-DMD research study update
This study is only open to boys in Scotland and although sufficient numbers of patients have been recruited in Glasgow, they are still recruiting from …
Ten posts in place to support UK clinical trial capacity – Newcastle plan
In December 2015, eight patient organisations, who are working to help support clinical trial development for Duchenne muscular dystrophy, announced a …
Ten posts in place to support UK clinical trial capacity – Newcastle planRead More
Access to Medicines and the Campaign for Translarna (Ataluren) timeline
Since the start of 2015, Action Duchenne campaigned tirelessly for Translarna (ataluren) to be made available, exerting maximum external pressure upon …
Access to Medicines and the Campaign for Translarna (Ataluren) timelineRead More
The fight for Translarna goes on – Action Duchenne in parliamentary session
In light of NHS England’s non-decision on Translarna last week, Action Duchenne shared a platform with the MPS Society in parliament yesterday …
The fight for Translarna goes on – Action Duchenne in parliamentary sessionRead More
