Dyne Therapeutics announced on the 20th of May, positive clinical data from its ongoing Phase 1/2 ACHIEVE trial of DYNE-101 in patients with myotonic …
Calling everyone from Scotland and Wales – Tell us what YOU think!
Tell us what YOU think We are contacting all of our families, clinicians, schools and care professionals across Scotland and Wales as we try to …
Calling everyone from Scotland and Wales – Tell us what YOU think!Read More
MHRA Translarna Survey
Introduction In 2014, the European Medicines Agency (EMA), granted a ‘Conditional Marketing Authorisation’ to Translarna for the treatment of …
PTC Therapeutics Announces European Commission Returns Translarna™ Opinion to CHMP For Re-evaluation
PTC Therapeutics has announced today that the European Commission (EC) has decided not to adopt the European Medicine Agency (EMA) Committee for …
Spring Webinar : BIND Study
The BIND project: Learning and behaviour challenges in Duchenne and Becker Muscular Dystrophies Join us on Wednesday 29th May at 5:30 pm for the …
Links and Resources
Here are some links to other charities and organisations who have been part of Yes I Can sessions, or that you might find useful. Pathfinders …
Science on Tour 2024 – Register your Interest
Behind the scenes at Action Duchenne, our Science Communication team have been working hard to put together 2024 Science on Tour Programme. The …
Spring Webinar – Dr Vasantha Gowda ‘DMD and Emergencies’
Join us on Saturday 11th May at 5pm for the next in our series of webinars. Dr Vasantha Gowda, consultant in paediatric neurology and neuromuscular …
Spring Webinar – Dr Vasantha Gowda ‘DMD and Emergencies’Read More
Annemeike Aartsma-Rus Webinar Recording
For anyone who missed the brilliant webinar hosted by Professor Annemeike Aartsma-Rus from 13th April 2024, this is the recording of her session. She …
Take part in a trial programme about behavioural and emotional difficulties
Andria Papageorgiou, postgraduate research student at The University of Surrey, is inviting you to take part in a 6 week programme for parents/carers …
Take part in a trial programme about behavioural and emotional difficultiesRead More
Introducing our Newest Trustee: Emma Simmonds
Introducing Our Newest Trustee: Emma Simmonds “On behalf of the Board of Trustees at Action Duchenne, I extend a warm welcometo Emma as our newest …
Join our NEW Online Support Groups
We decided our regular online support groups needed a bit of a re-think. To make sure we’ve got everyone covered, there are now going to be 4 …
