CEO's Message: Welcoming New Trustees and Farewell to Victoria PenriceAction Duchenne is delighted to announce the appointment of three distinguished …
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Submit Your Questions to be Answered by Pharmaceutical Companies
Yes I Can In-Person Meet-Up at Think Tank, Birmingham
Yes I Can In-Person Meet-Up at Think Tank, BirminghamWe are planning an in-person meet-up at Think Tank, the Science Museum in Birmingham. As well as …
Yes I Can In-Person Meet-Up at Think Tank, BirminghamRead More
The Committee for Medicinal Products for Human Use (CHMP) Issues Negative Opinion on Translarna™ Following European Commission Request for Review
PTC Therapeutics has announced that the European Medicine Agency (EMA) Committee for Medicinal Products for Human Use (CHMP) issued a negative …
Turning Point Families Day at Thomley
Turning Point Families Day at ThomleyOn Saturday 22nd June Dougie and I met up with other families at Thomley for the TurningPoint families …
A day to remember for Duchenne families with Alder Hey Children’s Hospital
On Thursday May 30th, we supported Alder Hey Children's Hospital hosting a special event for families affected by Duchenne muscular dystrophy (DMD). …
A day to remember for Duchenne families with Alder Hey Children’s HospitalRead More
Entrada Therapeutics Reports Positive Preliminary Data in Healthy Volunteers from Phase 1 ENTR-601-44-101 Trial for Duchenne Muscular Dystrophy
Entrada Therapeutics, a company developing treatments for rare diseases, reports encouraging preliminary data from a Phase 1 clinical trial …
Action Duchenne’s Science on Tour Team visit Ashford School
Action Duchenne Science on Tour Team visit Ashford SchoolA new addition to this years’ Science on Tour is our school visits, part of our ongoing …
Action Duchenne’s Science on Tour Team visit Ashford SchoolRead More
Make a Difference – Join Our Charity Running Events!
Are your employees ready to lace up their running shoes and support a great cause? 🌟 We invite your team to join us at one of our upcoming charity …
Make a Difference – Join Our Charity Running Events!Read More
Do you live in Scotland or Wales? Join our Focus Groups to tell us what support YOU need!
Do you live in Scotland or Wales? Join our Focus Groups to tell us what support YOU need!Improving the lives of everyone that lives with DMD is at the …
Do you live in Scotland or Wales? Join our Focus Groups to tell us what support YOU need!Read More
Sarepta Therapeutics Announces Positive Update on ELEVIDYS (delandistrogene moxeparvovec-rokl) Regulatory Progress for Duchenne Muscular Dystrophy (DMD)
Sarepta Therapeutics, Inc. today provided an update on the regulatory progress of ELEVIDYS (delandistrogene moxeparvovec-rokl), its gene therapy for …
Start your Summer as an AD Champion at the Parellel Windsor Festival of Inclusivity
Start your Summer as an Action Duchenne Champion Action Duchenne are proud to be a Parallel charity partner for their flagship Festival of …
Start your Summer as an AD Champion at the Parellel Windsor Festival of InclusivityRead More
