Action Duchenne is delighted to announce the appointment of Victoria Penrice as Company Secretary and trustee. Victoria is joining us at an exciting …
Jonathan raises the profile of Duchenne
Our amazing community have really got behind Jonathon Inkin singing his beautiful rendition of Jingle Bells. Jonathon is raising money for Action …
Duchenne Patient Academy in Athens
Last week our Trustee, Gary Fegan, was honoured to join delegates from Duchenne patient organisations from more than 40 countries worldwide …
Update on UNITE-DMD project
The UNITE-DMD project, which we are co-funding alongside Muscular Dystrophy UK and AFM-Téléthon brings together several strands of research to …
Duchenne Science events back on the road in 2020
We've welcomed over 100 people to our Science on Tour events throughout 2019, these empowering and invaluable sessions have been a huge success and we …
GA Solicitors – Charity of the Year
We were delighted to be chosen as Charity of the Year by Plymouth law firm GA Solicitors. As part of their fundraising the team organised …
A message from our Patron, Harry Hill
Harry Hill, one of our amazing Patrons, sent us a video which we proudly played at the Gala Dinner on Friday at the Action Duchenne International …
An unforgettable weekend at #ADCON19
Thank you to each and every person who attended the Action Duchenne International Conference 2019. We have all had such a wonderful weekend with …
Solid gene therapy trial placed on hold
Solid BioSciences has announced that the IGNITE DMD trial - a Phase I/II clinical trial of the company’s SGT-001 gene therapy - has been placed …
Thank you for helping us build a community
Wow, we've had a busy few weeks here at AD HQ, delivering one of our 3 key objectives of 'building a community'. Our team have barely touched the …
Roche halts development of myostatin inhibitor
Roche have announced the completion of a planned, interim analysis of the data from their trials of their myostatin inhibitor (called RG6206). The …
Vamorolone gains Promising Innovative Medicine status
We’re happy to announce that the MHRA (the medicines regulator in the UK) has given Promising Innovative Medicine (or PIM) status to Vamorolone as a …
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