After submitting a letter to No.10 Downing St on June 9, the Prime Minister David Cameron sent a host of replies to Action Duchenne yesterday to pass …
Access to Medicines and the Campaign for Translarna (Ataluren) timeline
Since the start of 2015, Action Duchenne campaigned tirelessly for Translarna (ataluren) to be made available, exerting maximum external pressure upon …
Access to Medicines and the Campaign for Translarna (Ataluren) timelineRead More
Action Duchenne working with Scottish Family to get Translarna approved by SMC
Ross Munro, living with Duchenne, was first enrolled on the PTC Therapeutics trial of Translarna in 2008, and has been in receipt of the …
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The fight for Translarna goes on – Action Duchenne in parliamentary session
In light of NHS England’s non-decision on Translarna last week, Action Duchenne shared a platform with the MPS Society in parliament yesterday …
The fight for Translarna goes on – Action Duchenne in parliamentary sessionRead More
Press release: First ever treatment for rare muscle wasting condition, Duchenne Muscular Dystrophy, given conditional approval by the European Commission
Children living with a genetic muscle wasting condition called Duchenne Muscular Dystrophy (DMD) have hope of a different future after the first ever …
