Searching for a cure, Improving lives
Welcome to the new Action Duchenne website! We’ve updated our site to make it easier to find the information you need, register for fundraising and parliamentary events and keep up to date with everything that’s going on at Action Duchenne. We will be adding more content over the next couple of months. If you have
Sarepta Therapeutics announced yesterday their plans to submit a new drug application (NDA) for eteplirsen to the US Food and Drug Administration (FDA) by the end of this year. Eteplirsen is Sarepta’s lead candidate to skip exon 51. The company have been in discussion with the regulatory agency since November 2013; when the FDA ruled
The Action Duchenne National Meeting 2014 will take place at Hereward College, Coventry CV4 9SW from 11-3pm on the 17th of May.
Key note speakers will talk about nutrition, respiratory care and ventilation in Duchenne.
Satchi Bill Google + Hangout today 4pm-4.40pm
Lord Saatchi and This Morning’s Dr Ranj will host a Google+ Hangout this afternoon to discuss..
Sarepta Therapeutics to Submit New Drug Application to FDA for Eteplirsen by the end of 2014
Sarepta Therapeutics announced yesterday their..